U.K. biotech Ikarovec has teamed up with VectorBuilder to work on an eye disease gene therapy that could be administered in a doctor’s office. Ikarovec’s IKAR-003 is currently in preclinical ...

An international team led by University of Manchester scientists has created the most detailed picture yet of how genetic differences shape the way the human eye works. The breakthrough could help ...

(Reuters) -MeiraGTx Holdings has signed a deal with Eli Lilly, potentially worth over $475 million, granting the pharma giant rights to its experimental gene therapy for a rare, inherited disorder ...

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...

Please provide your email address to receive an email when new articles are posted on . The biggest clinical disruptors in the ophthalmic market include developments in gene therapy and drug delivery.

A 6-year-old girl has had her sight restored thanks to a life-changing eye gene therapy on the NHS. Saffie Sandford from Stevenage in Hertfordshire was diagnosed with a rare inherited condition called ...

A genetic variant carried by at least one-fifth of the population may do far more than raise the odds of developing Alzheimer’s disease. New research argues that inheriting two copies of the APOE4 ...

To Ocugen CEO Shankar Musunuri, Ph.D., most gene therapy biotechs today lack vision. Rather than focusing on rare diseases with small patient populations, as Musunuri sees it, these companies should ...