A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College of Medicine and the UMass Chan Medical School have achieved ...

Cell and gene therapies use the body's building blocks - cells and genetic material - to boost the immune system or correct ...

News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, with a personalized CRISPR gene-editing therapy. The treatment corrects an ...

As we continue our series exploring genetic medicine, both in this story and in Destiny's Child No Longer: Rewriting Genetic Fate, gene therapy stands at a crossroads. On June 16, Sarepta Therapeutics ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College of Medicine and the UMass Chan Medical School have achieved ...

Cardiovascular disease is the world’s leading killer and one of the most economically damaging, as its prevalence and costs have been rising. According to our research, offering a one-time ...

Cell and gene therapy are revolutionary approaches to treating diseases at the molecular level. They involve the manipulation ...