Suneel Ram is a spiritual seeker, sings in a band and was the subject of a comic novel two years ago about living with Duchenne muscular dystrophy, a rare genetic ...

Managed Healthcare Executive gives C-suite executives in health plans and provider organizations news and strategies for ...

Patients in Scotland can't get the treatment - which is available in England - despite manufacturers giving it away for free ...

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...

Shares of Sarepta Therapeutics, Inc. (SRPT) traded over 2% lower in afternoon trade on Friday after the company said it has ...

Participants in the FORWARD-53 trial had clinically significant improvements in time-to-rise, among other metrics.

A federal advisory committee that provides guidance on which rare diseases newborns should be screened for has been dissolved ...

The Cambridge-based biotech's experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT) shared an update on Elevidys (delandistrogene moxeparvovec-rokl), the only approved ...

The European Medicines Agency asked for three clinical trials to be placed on hold until the exact cause of death of a US ...

Amid readouts from the Muscular Dystrophy Association’s annual meeting, the Clinical Trials Arena evaluates five DMD trials ...

Wave Life Sciences’ experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, setting the ...