Doing more to incorporate caregiver burden into value assessments and cost-effectiveness research of Duchene muscular dystrophy treatments was the focus of a recent International Society for ...

One of the demands raised during the protests was access to 'Elevidys', a one-time gene therapy treatment that has the ...

Managed Healthcare Executive gives C-suite executives in health plans and provider organizations news and strategies for ...

The European Medicines Agency asked for three clinical trials to be placed on hold until the exact cause of death of a US ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT) shared an update on Elevidys (delandistrogene moxeparvovec-rokl), the only approved ...

Muscular Dystrophy Association and Burn Boot Camp Team Up for the 9th Annual 'Be Their Muscle' Philanthropic Event ...

When her son reached three last year, a new name loomed over their lives — Duchenne Muscular Dystrophy (DMD), a ...

Defeat Duchenne Canada, the country's leading funder of Duchenne muscular dystrophy (DMD) research, is set to begin accepting innovative research proposals as of March 31, 2025. They are seeking ...

The Port St. Lucie Police Department fulfilled 10-year-old William Rivero's dream of becoming a police officer by swearing ...

Barry Byrne, MD, PhD, Powell Gene Therapy Center at the University of Florida, discusses gene therapy considerations for pediatric patients and how newborn screening can influence outcomes for ...